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Scott N. Freeman, Kathryn A. Burke, Menfo A. Imoisili, Timothy R. Coté 

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Presentation on theme: "Scott N. Freeman, Kathryn A. Burke, Menfo A. Imoisili, Timothy R. Coté "— Presentation transcript:

1 The Orphan Drug Act and the Development of Stem Cell-Based Products for Rare Diseases 
Scott N. Freeman, Kathryn A. Burke, Menfo A. Imoisili, Timothy R. Coté  Cell Stem Cell  Volume 7, Issue 3, Pages (September 2010) DOI: /j.stem Copyright © 2010 Elsevier Inc. Terms and Conditions

2 Figure 1 Orphan Product Applications, Designations, and Marketing Approvals and Stem Cell-Based Product Orphan Designations (A) The quantities of orphan product applications, designations, and approvals collectively from 1983–2009 stratified by year class intervals. (B) Stem cell-based product orphan designations by year from 1983–2009. Cell Stem Cell 2010 7, DOI: ( /j.stem ) Copyright © 2010 Elsevier Inc. Terms and Conditions

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